The global demand for Orphan Drugs Market is presumed to reach the market size of nearly USD 362.04 Billion by 2032 from USD 194.95 Billion in 2023 with a CAGR of 7.12% under the study period 2024 - 2032.
Orphan drugs are pharmaceutical medications created to treat rare diseases or conditions impacting a small number of individuals. Pharmaceutical companies often need to pay more attention to these diseases due to their limited patient populations and drug development and commercialization challenges. These drugs, including extended patent protection, tax credits, and accelerated approval processes, receive special regulatory incentives and market exclusivity to encourage their growth.
The increasing prevalence of rare diseases and disorders and advances in genetic research and diagnostic technologies drive the demand for orphan drugs targeting specific genetic mutations or rare conditions. Additionally, regulatory incentives and orphan drug designations granted by health authorities, such as the Orphan Drug Act in the United States and similar regulations in other countries, encourage pharmaceutical companies to invest in the research and development of orphan drugs. Furthermore, the growing patient advocacy and support groups for rare diseases are raising awareness and advocating for access to orphan drugs, driving demand and facilitating market growth. Moreover, advancements in biotechnology and drug development techniques, such as gene therapy, cell therapy, and precision medicine approaches, enable the development of innovative orphan drug therapies with improved efficacy and safety profiles.
Additionally, the increasing healthcare expenditure and insurance coverage for orphan drug treatments, combined with the growing acceptance of personalized medicine and value-based healthcare models, create favorable market conditions for orphan drug manufacturers. Furthermore, strategic collaborations and partnerships between pharmaceutical companies, academic institutions, and research organizations foster innovation and accelerate the development and commercialization of orphan drugs. However, increasing competition from alternative therapies and limited patient access may challenge the growth of the orphan drugs market in the coming years.
The research report covers Porter’s Five Forces Model, Market Attractiveness Analysis, and Value Chain analysis. These tools help to get a clear picture of the industry’s structure and evaluate the competition attractiveness at a global level. Additionally, these tools also give an inclusive assessment of each segment in the global market of orphan drugs. The growth and trends of orphan drugs industry provide a holistic approach to this study.
This section of the orphan drugs market report provides detailed data on the segments at country and regional level, thereby assisting the strategist in identifying the target demographics for the respective product or services with the upcoming opportunities.
By Disease Type
By Indicator
By Distribution Channel
This section covers the regional outlook, which accentuates current and future demand for the Orphan Drugs market across North America, Europe, Asia-Pacific, Latin America, and Middle East & Africa. Further, the report focuses on demand, estimation, and forecast for individual application segments across all the prominent regions.
The research report also covers the comprehensive profiles of the key players in the market and an in-depth view of the competitive landscape worldwide. The major players in the Orphan Drugs market include Novartis AG, Bristol-Myers Squibb Company, Celgene Corporation, F. Hoffmann-La Roche Ltd., Pfizer, Inc., Sanofi S.A., Alexion Pharmaceuticals, Inc., Eli Lilly and Company, Novo Nordisk A/S, AstraZeneca plc, Eisai Co., Ltd., Daiichi Sankyo Company Limited, Bayer AG, GlaxoSmithKline plc, Merck & Co., Inc., Johnson & Johnson. This section consists of a holistic view of the competitive landscape that includes various strategic developments such as key mergers & acquisitions, future capacities, partnerships, financial overviews, collaborations, new product developments, new product launches, and other developments.
1. PREFACE
1.1. Report Description
1.1.1 Objective
1.1.2 Target Audience
1.1.3 Unique Selling Proposition (USP) & offerings
1.2. Research Scope
1.3. Research Methodology
1.3.1 Market Research Process
1.3.2 Market Research Methodology
2. EXECUTIVE SUMMARY
2.1. Highlights of Market
2.2. Global Market Snapshot
3. ORPHAN DRUGS – INDUSTRY ANALYSIS
3.1. Introduction - Market Dynamics
3.2. Market Drivers
3.3. Market Restraints
3.4. Opportunities
3.5. Industry Trends
3.6. Porter’s Five Force Analysis
3.7. Market Attractiveness Analysis
3.7.1 Market Attractiveness Analysis By Disease Type
3.7.2 Market Attractiveness Analysis By Indicator
3.7.3 Market Attractiveness Analysis By Distribution Channel
3.7.4 Market Attractiveness Analysis By Region
4. VALUE CHAIN ANALYSIS
4.1. Value Chain Analysis
4.2. Raw Material Analysis
4.2.1 List of Raw Materials
4.2.2 Raw Material Manufactures List
4.2.3 Price Trend of Key Raw Materials
4.3. List of Potential Buyers
4.4. Marketing Channel
4.4.1 Direct Marketing
4.4.2 Indirect Marketing
4.4.3 Marketing Channel Development Trend
5. GLOBAL ORPHAN DRUGS MARKET ANALYSIS BY DISEASE TYPE
5.1. Overview By Disease Type
5.2. Historical and Forecast Data
5.3. Analysis By Disease Type
5.4. Oncology Historic and Forecast Sales By Regions
5.5. Gastrointestinal Historic and Forecast Sales By Regions
5.6. Pulmonary Historic and Forecast Sales By Regions
5.7. Neurology Historic and Forecast Sales By Regions
5.8. Hematology Historic and Forecast Sales By Regions
5.9. Cardiovascular Historic and Forecast Sales By Regions
5.10. Metabolic Disorders Historic and Forecast Sales By Regions
5.11. Endocrinology Historic and Forecast Sales By Regions
5.12. Infectious Diseases Historic and Forecast Sales By Regions
5.13. Othe...
